Minimal ureagenesis is necessary for survival in the murine model of hyperargininemia treated by AAV-based gene therapy
Hu C, Tai DS, Park H, Cantero G, Cantero-Nieto G, Chan E, Yudkoff M, Cederbaum SD, Lipshutz GS. Minimal ureagenesis is necessary for survival in the murine model of hyperargininemia treated by AAV-based gene therapy. Gene Ther. 2015 Feb;22(2):111-5. doi: 10.1038/gt.2014.106. Epub 2014 Dec 4. Erratum in: Gene Ther. 2015 Feb;22(2):216. PMID: 25474440; PMCID: PMC4320015.