23rd Annual American Society of Gene and Cell Therapy Conference

Matt, Suhail, and Jenna attended and presented their research at the 23rd Annual American Society of Gene and Cell Therapy (ASGCT) virtual Conference.


Matt’s poster presentation:

Nitzahn, M., Khoja, S., Lambert, J., Grisch-Chan, H. M., Thony, B., & Lipshutz, G. S., (2020).Minimal Protein from DNA Mini Circles Provides Therapeutic Benefit in CPS1 Deficiency. Abstract accepted for poster presentation at annual meeting of the American Society of Gene and Cell Therapy (ASGCT) in Boston, MA.

Jenna’s poster presentation:

Lambert, J. Liu, X., Khoja, S., Nitzahn, M., Eliav, A., Cederbaum, S., & Lipshutz, G. S., (2020). Oligodendrocyte Dysfunction and Global CNS Dysmyelination Occur in Arginase Deficiency that is Prevented with AAV-based Hepatic Gene Therapy. Abstract accepted for poster presentation at annual meeting of the American Society of Gene and Cell Therapy (ASGCT) in Boston, MA. Supplemental Figures

Suhail gave an oral presentation:

Khoja, S., Liu, X. B., Truong, B., Lambert, J., Eliav, A., Nitzahn, M., Zhu, X., Martini, P. G. V., & Lipshutz, G. S., (2020). Intermittent mRNA Therapy for Arginase Deficiency Results in Prevention of Dysmyelination of the Corticospinal Tract. Abstract accepted for oral presentation at annual meeting of the American Society of Gene and Cell Therapy (ASGCT) in Boston, MA