Long-term survival of the juvenile lethal arginase-deficient mouse with AAV gene therapy
Lee EK, Hu C, Bhargava R, Rozengurt N, Stout D, Grody WW, Cederbaum SD, Lipshutz GS. Long-term survival of the juvenile lethal arginase-deficient mouse with AAV gene therapy. Mol Ther. 2012 Oct;20(10):1844-51. doi: 10.1038/mt.2012.129. Epub 2012 Jul 3. PMID: 22760543; PMCID: PMC3464644.