Suhail Khoja PhD
Suhail Khoja Ph.D. is a Project Scientist in the Department of Surgery at UCLA. His research is primarily focused on CRISPR/Cas9-based correction of ARG1-deficient patient derived induced pluripotent stem cells and use this model to study the neuronal development in ARG1-deficient and ARG1 corrected cells. In addition Dr. Khoja is also investigating the correction of hepatic carbamoyl phosphate synthetase 1 (Cps1) deficiency in mice using In vivo gene therapy.
Besides his research, Dr. Khoja is nature lover and enjoys spending time and traveling with his family and friends
Xiao-Bo Liu PhD
Brian Truong BS
Brian is a PhD student in the Department of Molecular and Medical Pharmacology (2015-2019). His research has focused on developing human induced pluripotent stem cell-based gene therapy strategies for treatment of arginase deficiency. Additionally, with industry collaborators, he has also investigated lipid nanoparticle-encapsulated mRNA for treatment of arginase deficiency as well as other urea cycle disorders. During his free time, Brian enjoys kickboxing, lifting weights, and checking out the local nightlife.
Pharmacology home page: https://www.pharmacology.ucla.edu/
Matt Nitzahn BS
Matt is a PhD student in the Cell & Developmental Biology (CDB) home area of the Molecular Biology Interdepartmental Doctoral Program. His work focuses on designing and implementing novel gene- and cell-based therapies, including AAVs and CRISPR/Cas9, to treat urea cycle disorders, in particular CPS1 deficiency. During his free time, Matt enjoys reading fiction, cycling, and searching for the best pizza parlors in town.
Websites:
MBI home page: https://www.mbi.ucla.edu/
CDB home page: https://www.mbi.ucla.edu/cdb/
Jenna Lambert
Annie Chang
