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Lipshutz Lab Presentations at the 26th Annual American Society of Gene and Cell Therapy Conference

Lizzie Zhang and Dr. Gerry Lipshutz presented at this year’s ASGCT Conference. Lizzie presented “Oligodendrocyte Toxicity by Guanidino Compounds, Not Arginine, Fosters Dysmyelination in Arginase Deficiency and is Prevented by AAV-Based Gene Therapy.” Dr. Lipshutz presented “mRNA-3927 Therapy for Propionic Acidemia: Interim Data From a Phase 1/2 Study.” Congratulations to both Lizzie and Dr. Lipshutz!

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Lipshutz Lab receives new CIRM grant to develop stem-cell based therapies for SLC6a8 gene

Dr. Gerald Lipshutz has been awarded the Quest Award by the California Institute for Regenerative Medicine (CIRM)! The $2.3 million award will fund the lab’s work to develop a one-time gene therapy to treat creatine transporter deficiency, which inhibits creatine—a molecule that is an essential energy source for brain and muscle cells—from reaching the brain and muscles and causes neural…

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